Active, not recruitingPHASE1, PHASE2NCT06100276
Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants With SOD1 Amyotrophic Lateral Sclerosis (SOD1-ALS)
Studying Amyotrophic lateral sclerosis
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- UniQure Biopharma B.V.
- Principal Investigator
- Executive Director, Clinical DevelopmentUniQure Biopharma B.V.
- Intervention
- AMT-162(drug)
- Enrollment
- 20 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2024 – 2031
Study locations (12)
- Barrow Neurological Institute, Phoenix, Arizona, United States
- University of California Irvine, Irvine, California, United States
- California Pacific Medical Center, San Francisco, California, United States
- Mayo Clinic Florida, Jacksonville, Florida, United States
- Winship Cancer Institute of Emory University, Atlanta, Georgia, United States
- Northwestern University Feinberg School of Medicine, Chicago, Illinois, United States
- University of Kansas Medical Center, Fairway, Kansas, United States
- Massachusetts General Hospital, Sean M. Healey and AMG Center for ALS Research, Boston, Massachusetts, United States
- Mayo Clinic Rochester, Rochester, Minnesota, United States
- Columbia University Irving Medical Center, New York, New York, United States
- University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, United States
- Norrlands Universitetssjukhus, Umeå, Vasterbottens Ian, Sweden
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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