RecruitingNot applicableNCT06019637
A Long-term Safety Study in Brazilian Patients With a Diagnosis of Spinal Muscular Atrophy Treated With Zolgensma
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Novartis Pharmaceuticals
- Principal Investigator
- Novartis PharmaceuticalsNovartis Pharmaceuticals
- Intervention
- Onasemnogene Abeparvovec(other)
- Enrollment
- 50 enrolled
- Eligibility
- 0-100 years · All sexes
- Timeline
- 2023 – 2038
Study locations (2)
- Novartis Investigative Site, Curitiba, Paraná, Brazil
- Novartis Investigative Site, São Paulo, São Paulo, Brazil
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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