Active, not recruitingPhase 2NCT05794139
Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- NMD Pharma A/S
- Intervention
- NMD670(drug)
- Enrollment
- 54 enrolled
- Eligibility
- 18-75 years · All sexes
- Timeline
- 2023 – 2026
Study locations (30)
- UCLA David Geffen School Of Medicine - Neurology, Los Angeles, California, United States
- Stanford University Medical Center, Palo Alto, California, United States
- University of Colorado Neurology Clinic, Aurora, Colorado, United States
- UF Fixel Institute for Neurological Diseases, Gainesville, Florida, United States
- Rare Disease Center, Atlanta, Georgia, United States
- University of Kansas Medical Center, Kansas City, Kansas, United States
- The Johns Hopkins Medicine, Spinal Muscular Atrophy Center, Baltimore, Maryland, United States
- Roy Blunt NextGen Precision Health Institute, Columbia, Missouri, United States
- Washington University School of Medicine, St Louis, Missouri, United States
- Rare Disease Research - Raleigh-Durham, Hillsborough, North Carolina, United States
- The Ohio State University Wexner Medical Center, Columbus, Ohio, United States
- Neurology Rare Disease Center, Denton, Texas, United States
- UZ Leuven - Neurochirurgie Campus Gasthuisberg, Leuven, Belgium
- CHR de la Citadelle - Neurologie, Liège, Belgium
- Heritage Medical Research Clinic, Calgary, Canada
- +15 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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