Personalized Medicine for SMA: a Translational Project

Key facts

Sponsor

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Principal Investigator

Eugenio Mercuri, MD

F Policlinico Gemelli IRCCS

Enrollment

90 enrolled

Eligibility

All sexes

Timeline

2021 – 2024

Study locations (2)

• Ospedale Bambino gesu, Rome, Italy
• Policlinico gemelli, Rome, Italy

Collaborators

University of Milan · Ospedale Pediatrico Bambino Gesu

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Other trials for Autosomal dominant adult-onset proximal spinal muscular atrophy

Additional recruiting or active studies for the same condition.

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See all trials for Autosomal dominant adult-onset proximal spinal muscular atrophy →