Active, not recruitingNot applicableNCT06419322

Acceptability, Feasibility, Safety and Efficacy of a Optimized Rehabilitation Program for Treated Patients With Spinal Muscular Atrophy (SMA).

Studying Autosomal dominant adult-onset proximal spinal muscular atrophy

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Key facts

Sponsor
University of Oxford
Principal Investigator
Charlotte Lilien
University of Oxford, Department of Paediatrics
Intervention
Optimized rehabilitation program(other)
Enrollment
14 enrolled
Eligibility
1-10 years · All sexes
Timeline
20242026

Study locations (1)

Collaborators

Oxford Brookes University · Oxford University Hospitals NHS Trust · ACE SMA Charity · Roche Products Limited · Scholar Rock, Inc. · Biohaven Therapeutics Ltd. · Rally Round Rupert Charity

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT06419322 on ClinicalTrials.gov

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