Enrolling by invitationPHASE1, PHASE2NCT05614531
Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients with Spinal Muscular Atrophy Type 1
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Guangzhou Jiayin Biotech Ltd
- Intervention
- EXG001-307 injection(genetic)
- Enrollment
- 12 enrolled
- Eligibility
- All sexes
- Timeline
- 2023 – 2025
Study locations (2)
- The Children's Hospital of Fudan University, Shanghai, Shanghai Municipality, China
- The Children'S Hospital Zhejiang University of Medicine, Hangzhou, Zhejiang, China
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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