Active, not recruitingPhase 3NCT05337553
A Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Biohaven Pharmaceuticals, Inc.
- Principal Investigator
- Lindsey Lair, MDBiohaven Pharmaceuticals, Inc.
- Intervention
- taldefgrobep alfa(drug)
- Enrollment
- 269 enrolled
- Eligibility
- 4-21 years · All sexes
- Timeline
- 2022 – 2026
Study locations (30)
- Phoenix Children's, Phoenix, Arizona, United States
- UCSD & Rady Children's, La Jolla, California, United States
- Children's Hospital of Los Angeles, Los Angeles, California, United States
- UCSF Benioff Children's Hospital, Medical Center, San Francisco, California, United States
- Children's Hospital Colorado, Aurora, Colorado, United States
- UF Health, Shands Hospital, Gainesville, Florida, United States
- Rare Disease Research, Atlanta, Georgia, United States
- Northwestern University - Feinberg School of Medicine - Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- Indiana University -Riley Research, Indianapolis, Indiana, United States
- University of Iowa, Iowa City, Iowa, United States
- University of Kansas Medical Center, Fairway, Kansas, United States
- Boston Children's Hospital - Harvard, Boston, Massachusetts, United States
- BSHS Office of Research, Grand Rapids, Michigan, United States
- Washington University in St. Louis, St Louis, Missouri, United States
- Columbia University Medical Center, New York, New York, United States
- +15 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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