Active, not recruitingPhase 2NCT05115110
A Study to Investigate the Safety and Efficacy of RO7204239 in Combination With Risdiplam (RO7034067) in Participants With Spinal Muscular Atrophy
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Hoffmann-La Roche
- Principal Investigator
- Clinical TrialsHoffmann-La Roche
- Intervention
- RO7204239(drug)
- Enrollment
- 259 enrolled
- Eligibility
- 2-25 years · All sexes
- Timeline
- 2022 – 2029
Study locations (20)
- Nemours Children's Hospital, Orlando, Florida, United States
- Boston Childrens Hospital, Boston, Massachusetts, United States
- Columbia University Medical Center, New York, New York, United States
- Neurology & Neuromuscular Care Center, Flower Mound, Texas, United States
- Sydney Children's Hospital, Randwick, New South Wales, Australia
- UZ Gent, Ghent, Belgium
- Chr de La Citadelle, Liège, Belgium
- British Columbia Children's Hospital, Vancouver, British Columbia, Canada
- The Hospital for Sick Children, Toronto, Ontario, Canada
- McGill University Health Centre - Glen Site, Montreal, Quebec, Canada
- Clinical Hospital Centre Zagreb, Zagreb, Croatia
- Ospedale Pediatrico Bambino Gesù, Rome, Lazio, Italy
- Policlinico Agostino Gemelli, Rome, Lazio, Italy
- IRCCS Istituto Giannina Gaslini, Genoa, Liguria, Italy
- Fondazione IRCCS Istituto Neurologico ?Carlo Besta?, Milan, Lombardy, Italy
- +5 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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