RecruitingNCT04177134

French Register of Patients With Spinal Muscular Atrophy

Studying Autosomal dominant adult-onset proximal spinal muscular atrophy

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Key facts

Sponsor
Assistance Publique - Hôpitaux de Paris
Principal Investigator
Susana Quijano-Roy, MD, PhD
Unité neuromusculaire, Service de Neurologie et Réanimation Pédiatrique, Hôpital Raymond Poincaré, 92380 Garches, FRANCE
Enrollment
1000 enrolled
Eligibility
All sexes
Timeline
20202029

Study locations (1)

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT04177134 on ClinicalTrials.gov

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