TerminatedPHASE1, PHASE2NCT04145037
Lentiviral Vector Gene Therapy - The Guard1 Trial of AVR-RD-02 for Subjects With Type 1 Gaucher Disease
Studying Gaucher disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- AVROBIO
- Principal Investigator
- Milena Veselinovic, MDAVROBIO
- Intervention
- AVR-RD-02(drug)
- Enrollment
- 8 enrolled
- Eligibility
- 18-50 years · All sexes
- Timeline
- 2019 – 2023
Study locations (5)
- University of California San Diego, San Diego, California, United States
- University of Iowa, Iowa City, Iowa, United States
- Hackensack University Medical Center, Hackensack, New Jersey, United States
- UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
- University Health Network, Toronto, Ontario, Canada
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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