Clinical trials for Gaucher disease
13 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- ACTIVE NOT RECRUITINGEarly Phase 1NCT06528080A Clinical Study for the Treatment of Pediatric and Adolescent Patients With Type 1 Gaucher DiseaseShanghai Jiao Tong University School of Medicine · PI: xiumin wang, PhD
- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT06545136Long Term Follow-up Study of Type-1 Gaucher Subjects Post FLT201 Dose (GALILEO-2)Spur Therapeutics
- ACTIVE NOT RECRUITINGNCT06488261Long Term Follow-Up for Safety of AVR-RD-02John Bernat · PI: John A. Bernat, MD, PhD
- RECRUITINGN/ANCT05992532GammaGA: Prevalence of Acid Sphingomyelinase Deficiency Disease (ASMD) and Gaucher Disease in Patients With Monoclonal Gammopathies and/or Multiple MyelomaFundación Española de Hematología y Hemoterapía · PI: FEHH SEHH, MD
- RECRUITINGN/ANCT05843552Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher DiseaseUniversity of Minnesota · PI: Reena Kartha, PhD, MS
- RECRUITINGEarly Phase 1NCT06272149An Exploratory Clinical Trial of VGN-R08b in Patients With Type II Gaucher DiseaseXinhua Hospital, Shanghai Jiao Tong University School of Medicine · PI: Zhang Huiwen, Dr.
- RECRUITINGPhase 1NCT05487599A Clinical Trial of PR001 (LY3884961) in Patients With Peripheral Manifestations of Gaucher Disease (PROCEED)Prevail Therapeutics · PI: Sarah Neuhaus, DO
- ACTIVE NOT RECRUITINGNCT05526664Omics Gaucher Study: Multiomic ApproachCENTOGENE GmbH Rostock · PI: Peter Bauer, MD
- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT04411654Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE)Prevail Therapeutics · PI: Hamzeh Migdadi, M.D.
- RECRUITINGNCT03190837A Long-term Follow-up Study of Gaucher DiseaseDuke University · PI: Priya Kishnani, MD
- RECRUITINGN/ANCT03291223Gaucher Disease Outcome Survey (GOS)Shire · PI: Shire Study Physician
- ENROLLING BY INVITATIONN/ANCT00001215Genetic Studies of Lysosomal Storage DisordersNational Human Genome Research Institute (NHGRI) · PI: Ellen Sidransky, M.D.
- RECRUITINGN/ANCT00358943International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registryGenzyme, a Sanofi Company · PI: Study Director