Active, not recruitingEarly Phase 1NCT06528080
A Clinical Study for the Treatment of Pediatric and Adolescent Patients With Type 1 Gaucher Disease
Studying Gaucher disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Shanghai Jiao Tong University School of Medicine
- Principal Investigator
- xiumin wang, PhDShanghai Children's Medical Center, School of Medicine, Shanghai Jiao Tong University
- Intervention
- LY-M001(genetic)
- Enrollment
- 9 enrolled
- Eligibility
- 6-18 years · All sexes
- Timeline
- 2024 – 2027
Study locations (1)
- Shanghai Children's Medical Center, School of Medicine, Shanghai Jiao Tong University, Shanghai, Shanghai Municipality, China
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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