Active, not recruitingPhase 3NCT04042025
Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Novartis Gene Therapies
- Principal Investigator
- Sitra Tauscher-Wisniewski, MDNovartis Gene Therapies, Inc.
- Intervention
- Onasemnogene Abeparvovec-xioi(biological)
- Enrollment
- 85 enrolled
- Eligibility
- All sexes
- Timeline
- 2020 – 2035
Study locations (20)
- Stanford University Medical Center, Palo Alto, California, United States
- Children's Hospital Colorado, Aurora, Colorado, United States
- Ann Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- John Hopkins Hospital - David M. Rubenstein Child Health Building, Baltimore, Maryland, United States
- Massachusetts General Hospital, Boston, Massachusetts, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- Spectrum Health Hospitals Helen DeVos Children's Hospital, Grand Rapids, Michigan, United States
- Washington Unviersity School of Medicine in Saint Louis, St Louis, Missouri, United States
- Columbia University Medical Center, New York, New York, United States
- Duke University, Durham, North Carolina, United States
- Nationwide Children's Hospital, Columbus, Ohio, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- Clinic for Special Children, Strasburg, Pennsylvania, United States
- Children's Health Specialty Center Dallas Campus, Dallas, Texas, United States
- University of Utah Health, Salt Lake City, Utah, United States
- +5 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT04042025 on ClinicalTrials.govOther trials for Spinal Muscular Atrophy
Additional recruiting or active studies for the same condition.
- RECRUITINGNANCT07488338HABIT-ILE + FST in Children With SMA: Preliminary EffectivenessTeachers College, Columbia University
- RECRUITINGNCT07400198Gait and Bone Health in SMAJacqueline Montes
- RECRUITINGPHASE1, PHASE2NCT07070999Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1Gemma Biotherapeutics
- RECRUITINGNANCT07321977Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic VolunteersInstitut de Myologie, France
- RECRUITINGPHASE2NCT07287982A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophyargenx
- RECRUITINGNANCT07286565Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn ScreeningCentre Hospitalier Universitaire de Liege
- RECRUITINGNCT06532474Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed TherapiesSt. Jude Children's Research Hospital
- RECRUITINGPHASE3NCT07265232Real World Clinical Effectiveness & Safety of Vesemnogene Lantuparvovec for Spinal Muscular Atrophy (SMA) in Low-middle Income Countries (LMIC).Lantu Biopharma