Active, not recruitingNot applicableNCT03709784
Spinraza in Adult Spinal Muscular Atrophy
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Washington University School of Medicine
- Principal Investigator
- Craig Zaidman, MDWashington University School of Medicine
- Intervention
- Observational study to examine safety, tolerability, and effectiveness of SPINRAZA® prescribed as part of standard of care(drug)
- Enrollment
- 148 enrolled
- Eligibility
- 18-70 years · All sexes
- Timeline
- 2018 – 2024
Study locations (11)
- Barrow Neurological Institute, Phoenix, Arizona, United States
- Georgetown University, Washington D.C., District of Columbia, United States
- Johns Hopkins, Baltimore, Maryland, United States
- Massachusetts General Hospital-Harvard University, Boston, Massachusetts, United States
- Memorial Healthcare, Owosso, Michigan, United States
- Washington University School of Medicine, St Louis, Missouri, United States
- New York University School of Medicine, New York, New York, United States
- Houston Methodist Neurological Institute, Houston, Texas, United States
- Children's Hospital of the King's Daughthers, Norfolk, Virginia, United States
- University of Washington, Seattle, Washington, United States
- Montreal Neurological Institute and Hospital, Montreal, Quebec, Canada
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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