SRT in Comparison to ERT on Immune Aspects and Bone Involvement in Gaucher Disease

Key facts

Sponsor

Lysosomal and Rare Disorders Research and Treatment Center, Inc.

Principal Investigator

Ozlem Goker-Alpan, MD

Study Principle Investigator

Enrollment

30 enrolled

Eligibility

18 years · All sexes

Timeline

2015 – 2020

Study locations (1)

• O&O Alpan, LLC, Fairfax, Virginia, United States

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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See all trials for Gaucher disease →