CompletedPhase 1NCT02122952
Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1
Studying Spinal Muscular Atrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Novartis Gene Therapies
- Principal Investigator
- Jerry R Mendell, MDNationwide Children's Hospital
- Intervention
- AVXS-101(biological)
- Enrollment
- 15 enrolled
- Eligibility
- All sexes
- Timeline
- 2014 – 2017
Study locations (1)
- Nationwide Children's Hospital, Columbus, Ohio, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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