CompletedPHASE1, PHASE2NCT01395641
A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC
Studying Aromatic L-amino acid decarboxylase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- National Taiwan University Hospital
- Principal Investigator
- Wuh-Liang Hwu, M.D., Ph.D.National Taiwan University Hospital
- Intervention
- gene therapy(drug)
- Enrollment
- 10 enrolled
- Eligibility
- All sexes
- Timeline
- 2014 – 2022
Study locations (1)
- National Taiwan University Hospital, Taipei, Taiwan
Collaborators
PTC Therapeutics
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT01395641 on ClinicalTrials.govOther trials for Aromatic L-amino acid decarboxylase deficiency
Additional recruiting or active studies for the same condition.
- ACTIVE NOT RECRUITINGPHASE1NCT06432140A Trial to Evaluate Safety and Efficacy of a Product Named VGN-R09b in Severe AADC DeficiencyShanghai Vitalgen BioPharma Co., Ltd.
- RECRUITINGEARLY PHASE1NCT05765981An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.Shanghai Jiao Tong University School of Medicine
- ACTIVE NOT RECRUITINGPHASE2NCT04903288A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric ParticipantsPTC Therapeutics
- RECRUITINGPHASE1NCT02852213A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric PatientsKrzysztof Bankiewicz
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