Active, not recruitingPhase 2NCT04903288
A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric Participants
Studying Aromatic L-amino acid decarboxylase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- PTC Therapeutics
- Intervention
- Eladocagene Exuparvovec(genetic)
- Enrollment
- 13 enrolled
- Eligibility
- 1-17 years · All sexes
- Timeline
- 2021 – 2028
Study locations (6)
- Boston Children's Hospital, Boston, Massachusetts, United States
- Duke University Hospital, Durham, North Carolina, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- Texas Children's Hospital, Houston, Texas, United States
- Chaim Sheba Medical Center, Ramat Gan, Israel
- National Taiwan University Hospital, Department of Pediatrics and Medical Genetics, Taipei, Taiwan
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT04903288 on ClinicalTrials.govOther trials for Aromatic L-amino acid decarboxylase deficiency
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- RECRUITINGEARLY PHASE1NCT05765981An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.Shanghai Jiao Tong University School of Medicine
- RECRUITINGPHASE1NCT02852213A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric PatientsKrzysztof Bankiewicz
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