Clinical trials for Aromatic L-amino acid decarboxylase deficiency
4 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- ACTIVE NOT RECRUITINGPhase 1NCT06432140A Trial to Evaluate Safety and Efficacy of a Product Named VGN-R09b in Severe AADC DeficiencyShanghai Vitalgen BioPharma Co., Ltd. · PI: Xiumin Wang, MD
- RECRUITINGEarly Phase 1NCT05765981An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.Shanghai Jiao Tong University School of Medicine · PI: Jiwen Wang, Doctor
- ACTIVE NOT RECRUITINGPhase 2NCT04903288A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric ParticipantsPTC Therapeutics
- RECRUITINGPhase 1NCT02852213A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric PatientsKrzysztof Bankiewicz · PI: Krystof Bankiewicz, MD, PhD