CompletedNCT01136304
Validating a New Severity Score System for Adults With Type 1 Gaucher Disease (GD1)
Studying Gaucher disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- University Research Foundation for Lysosomal Storage Diseases, Inc.
- Principal Investigator
- Neal J Weinreb, MDUniversity Research Foundation for Lysosomal Storage Diseases, Inc.
- Intervention
- Imiglucerase(drug)
- Enrollment
- 173 enrolled
- Eligibility
- 18 years · All sexes
- Timeline
- 2010 – 2013
Study locations (2)
- Tower Cancer Research Foundation, Beverly Hills, California, United States
- Northwest Oncology Hematology Associates PA, Coral Springs, Florida, United States
Collaborators
University of Pittsburgh
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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