Clinical Study to Evaluate the Long Term Efficacy, Safety and Tolerability of Miglustat in Patients With Stable Type 1 Gaucher Disease

Key facts

Sponsor

Actelion

Principal Investigator

Timothy Cox, Prof

University of Cambridge

Intervention

Miglustat(drug)

Enrollment

42 enrolled

Eligibility

18 years · All sexes

Timeline

2006 – 2010

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

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