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2 articles from the last 90 days matching "vascular diseases"

Clinical trialUNITERAREApr 3

New Recruiting Trial: A Phase 1 Study of PRT12396 in Participants With Select Myeloproliferative Neoplasms

Prelude Therapeutics is testing a new drug called PRT12396 in people with certain blood cancers called myeloproliferative neoplasms. This is an early-stage study (Phase 1) to see if the drug is safe and how it works in the body. The study is now accepting patients and is expected to start in April 2026.

WHY IT MATTERSThis trial offers access to a potentially new treatment option for patients with myeloproliferative neoplasms who may have limited alternatives, particularly if they have specific subtypes targeted by this drug.
💬 Ask your doctorMyeloproliferative neoplasmsPolycythemia veraEssential thrombocythemiaRead →
Clinical trialCLINICALTRIALSMar 26

Trial Now Recruiting: Pregnancy in Women With Rare Multisystemic Vascular Diseases: COGRare5 Study (NCT04194619)

Researchers are looking for pregnant women or women planning to get pregnant who have rare blood vessel diseases like Hereditary Hemorrhagic Telangiectasia, Marfan syndrome, lymphedema, or arteriovenous malformations. This study will track their pregnancies to understand what complications might happen for the mother and baby, since doctors don't have good information about this yet.

WHY IT MATTERSThis is the first large study to prospectively track pregnancy outcomes in women with these rare vascular diseases, filling a critical gap in medical knowledge that could directly improve care and safety for pregnant patients with these conditions.
→ You can act on thisHereditary Hemorrhagic TelangiectasiaMarfan SyndromePrimary LymphedemaRead →

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