Systemic mastocytosis with associated hematologic neoplasm

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1FDA treatments22Specialists8Treatment centers2Financial resources

Where are you in your journey?

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Also known as:

SM-AHNMDSystemic mastocytosis with an associated clonal hematologic non-mast cell lineage diseaseSM-AHN

Clinical phenotype terms— hover any for plain English:

Hematological neoplasmHP:0004377Myeloid leukemiaHP:0012324Elevated total serum tryptaseHP:0031901Abnormal mast cell morphologyHP:0100494Normochromic anemiaHP:0001895Normocytic anemiaHP:0001897Myeloproliferative disorderHP:0005547Bone marrow hypercellularityHP:0031020
Orphanet ↗NORD ↗

FDA & Trial Timeline

1 event
Oct 2003

Radiogardase: FDA approved

Treatment of patients with known or suspected internal contamination with radioactive cesium and/or radioactive or non-radioactive thallium to increase their rates of elimination

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

1 available

Rydapt

RYDAPT· Novartis Pharmaceuticals Corporation

indicated for the treatment of adult patients with systemic mastocytosis with associated hematological neoplasm (SM-AHN)

View Details →FDA Label ↗Patient Assistance ↗

Clinical Trials

View all trials with filters →

No actively recruiting trials found for Systemic mastocytosis with associated hematologic neoplasm at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Systemic mastocytosis with associated hematologic neoplasm community →

Specialists

22 foundView all specialists →
AM
Andrew Kuykendall, MD
DALLAS, TX
Specialist
PI on 2 active trials
BS
Brenda Sandmaier
SEATTLE, WA
Specialist
PI on 17 active trials
KM
Kyoo H. Lee, MD
Specialist
PI on 8 active trials
MF
Maryam Fouladi
COLUMBUS, OH
Specialist
PI on 7 active trials2 Systemic mastocytosis with associated hematologic neoplasm publications
RN
Ryotaro Nakamura
Duarte, California
Specialist

Rare Disease Specialist

PI on 6 active trials
RP
Rachael Easton, MD, Ph.D.
TROY, MI
Specialist
PI on 1 active trial
NR
Nancy Wells, DNSc, RN
Specialist
PI on 2 active trials
JG
Jason Gotlib
PALO ALTO, CA
Specialist
PI on 2 active trials6 Systemic mastocytosis with associated hematologic neoplasm publications
JM
Jeffrey J. Raizer, MD
CHICAGO, IL
Specialist
PI on 7 active trials
JD
John Deeken
FAIRFAX, VA
Specialist
PI on 1 active trial
AP
Anthony L Boral, MD, PhD
CAMBRIDGE, MA
Specialist
PI on 1 active trial
SP
Suzanne C. Danhauer, PhD
WINSTON SALEM, NC
Specialist
PI on 5 active trials
TM
Tom R. Fitch, M.D.
GLENDALE, AZ
Specialist
PI on 1 active trial
NM
Neal J. Meropol, MD
BROOKLYN, NY
Specialist
PI on 1 active trial
MM
Mary Ann Knovich, MD
CHARLOTTE, NC
Specialist
PI on 1 active trial
RP
Robert Z. Orlowski, MD, PhD
HOUSTON, TX
Specialist
PI on 1 active trial
HM
Hyman Muss, MD
CHAPEL HILL, NC
Specialist
PI on 2 active trials
AP
Anthony F. Shields, MD, PhD
Specialist
PI on 1 active trial
PM
Paul Armistead, MD
CHAPEL HILL, NC
Specialist
PI on 1 active trial
EM
Elizabeth C. Dees, MD
CHAPEL HILL, NC
Specialist
PI on 1 active trial
AM
Adam J. Esbenshade, MD
NASHVILLE, TN
Specialist
PI on 2 active trials
RR
Regan Demshar, RN
CLEVELAND, OH
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center ↗

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center ↗

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program ↗

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site ↗

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site ↗

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site ↗

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine ↗

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program ↗

UCLA Health

📍 Los Angeles, CA

Financial Resources

2 resources
Rydapt(RYDAPT)— Novartis Pharmaceuticals Corporation

Radiogardase

Heyl Chemisch-Pharmzeutische Fabrik GMBH & Co, KG

Radiogardase — Contact Heyl Chemisch-Pharmzeutische Fabrik GMBH & Co, KG

Unverified — confirm before calling
Patient Assistance
Manufacturer Program
Accepting applications

Travel Grants

No travel grants are currently matched to Systemic mastocytosis with associated hematologic neoplasm.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Systemic mastocytosis with associated hematologic neoplasm

No recent news articles for Systemic mastocytosis with associated hematologic neoplasm.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Systemic mastocytosis with associated hematologic neoplasm

Which specialists treat Systemic mastocytosis with associated hematologic neoplasm?

22 specialists and care centers treating Systemic mastocytosis with associated hematologic neoplasm are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Systemic mastocytosis with associated hematologic neoplasm?

2 patient support programs are currently tracked on UniteRare for Systemic mastocytosis with associated hematologic neoplasm. See the treatments and support programs sections for copay assistance, eligibility, and contact details.