Rare ovarian cancer

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7FDA treatments1Active trials9Specialists8Treatment centers2Financial resources

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Rare ovarian cancer encompasses a heterogeneous group of uncommon malignant tumors arising from the ovary that do not fall into the category of common epithelial ovarian carcinomas (such as high-grade serous carcinoma). This broad category includes several distinct histological subtypes such as small cell carcinoma of the ovary (hypercalcemic type), ovarian clear cell carcinoma, low-grade serous carcinoma, mucinous ovarian carcinoma, granulosa cell tumors, Sertoli-Leydig cell tumors, ovarian carcinosarcoma, and other rare subtypes. Each subtype has distinct molecular, clinical, and prognostic features. These cancers primarily affect the female reproductive system but can spread to the peritoneum, lymph nodes, liver, lungs, and other organs. Symptoms of rare ovarian cancers are often nonspecific and may include abdominal or pelvic pain, bloating, early satiety, changes in bowel or bladder habits, unexplained weight loss, and an abdominal mass. Some subtypes present with specific features; for example, small cell carcinoma of the ovary (hypercalcemic type) often presents in young women with elevated serum calcium levels, while granulosa cell tumors may produce estrogen leading to abnormal uterine bleeding or precocious puberty in children. Diagnosis typically involves imaging, serum tumor markers, and histopathological examination of tissue obtained through surgery. Treatment approaches vary by subtype but generally include surgical debulking (cytoreductive surgery) as a cornerstone, often combined with platinum-based chemotherapy. Due to the rarity of these tumors, evidence-based treatment guidelines are limited, and management is frequently extrapolated from data on more common ovarian cancers or based on small case series and expert consensus. Emerging targeted therapies and immunotherapies are being investigated in clinical trials for specific subtypes. Prognosis varies widely depending on the histological subtype, stage at diagnosis, and response to treatment. Multidisciplinary care at specialized centers with experience in rare gynecological cancers is strongly recommended.

Also known as:

Inheritance

Multifactorial

Caused by a mix of several genes and environmental factors

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

FDA & Trial Timeline

7 events
Mar 2026ZEJULA: New indication approved
FDAcompleted
Nov 2022

Elahere: FDA approved

treatment of adult patients with folate receptor-alpha (FR?) positive, platinum-resistant epithelial ovarian, fallopian tube, or primary peritoneal cancer, who have received one to three prior systemic treatment regimens. Select patients for therapy based on an FDA-approved test.

FDAcompleted
Oct 2021A Study Evaluating the Efficacy and Safety of Biomarker-Driven Therapies in Patients With Persistent or Recurrent Rare Epithelial Ovarian Tumors

Hoffmann-La Roche — PHASE2

TrialACTIVE NOT RECRUITING
Apr 2018

Rubraca: FDA approved

For the maintenance treatment of adult patients with recurrent epithelial ovarian, fallopian tube, or primary peritoneal cancer who are in complete or partial response to platinum-based chemotherapy.

FDAcompleted
Aug 2017

Lynparza: FDA approved

Maintenance treatment of adult patients with recurrent epithelial ovarian, fallopian tube or primary peritoneal cancer, who are in a complete or partial response to platinum-based chemotherapy.

FDAcompleted
Mar 2017

Zejula: FDA approved

Indicated for maintenance treatment of adult patients with recurrent epithelial ovarian, fallopian tube, or primary peritoneal cancer who are in a complete or partial response to platinum-based chemotherapy

FDAcompleted
Sep 1996

Gliadel: FDA approved

As an adjunct to surgery to prolong survival in patients with recurrent glioblastoma multiforme for whom surgical resection is indicated

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

7 available

Oncoscint CR/OV

Satumomab pendetide· Cytogen Corporation

For determining the extent and location of extraphepatic malignant disease in patients with known ovarian cancer

Doxil

doxorubicin HCL liposome injection· Johnson & Johnson Pharmaceutical Research & Dev.■ Boxed Warning

indicated for the treatment of patients with ovarian cancer whose disease has progressed or recurred after platinum-based chemotherapy

Elahere

mirvetuximab soravtansine-gynx· ImmunoGen, Inc.■ Boxed WarningOrphan Drug
treatment of adult patients with folate receptor-alpha (FR?) positive, platinum-resistant epithelial ovarian, fallopian tube, or primary peritoneal cancer, who have received one to three prior systemi

treatment of adult patients with folate receptor-alpha (FR?) positive, platinum-resistant epithelial ovarian, fallopian tube, or primary peritoneal cancer, who have received one to three prior systemic treatment regimens. Select patients for therapy based on an FDA-approved test.

Rubraca

rucaparib· pharma&Orphan Drug

For the maintenance treatment of adult patients with recurrent epithelial ovarian, fallopian tube, or primary peritoneal cancer who are in complete or partial response to platinum-based chemotherapy.

Lynparza

olaparib· AstraZeneca Pharmaceuticals LPOrphan Drug

Maintenance treatment of adult patients with recurrent epithelial ovarian, fallopian tube or primary peritoneal cancer, who are in a complete or partial response to platinum-based chemotherapy.

Zejula

niraparib· GlaxoSmithKline, LLC.Orphan Drug
Indicated for maintenance treatment of adult patients with recurrent epithelial ovarian, fallopian tube, or primary peritoneal cancer who are in a complete or partial response to platinum-based chemot

Indicated for maintenance treatment of adult patients with recurrent epithelial ovarian, fallopian tube, or primary peritoneal cancer who are in a complete or partial response to platinum-based chemotherapy

Gliadel

polifeprosan 20 with carmustine· Guilford Pharmaceuticals, Inc.Orphan Drug

As an adjunct to surgery to prolong survival in patients with recurrent glioblastoma multiforme for whom surgical resection is indicated

Clinical Trials

1 recruitingView all trials with filters →
Phase 21 trial
A Study Evaluating the Efficacy and Safety of Biomarker-Driven Therapies in Patients With Persistent or Recurrent Rare Epithelial Ovarian Tumors
Phase 2
Active Prior treatment eligible
PI: Clinical Trials (Hoffmann-La Roche) · Sites: San Francisco, California; St Louis, Missouri +18 more · Age: 1899 yrs

Specialists

9 foundView all specialists →
JM
Jurgen Mulsow, Mr.
Dublin
Specialist

Rare Disease Specialist

EP
Els Van Nieuwenhuysen, MD PhD
Specialist
PI on 1 active trial
SP
Sandip P Patel
Birmingham, Alabama
Specialist

Rare Disease Specialist

PI on 1 active trial
CD
Camila MV Moniz, Doctor
SAN ANTONIO, TX
Specialist
PI on 1 active trial
FJ
Florence JOLY
Specialist
PI on 1 active trial26 Rare ovarian cancer publications
MM
Michael Heinrich, MD
Specialist
PI on 1 active trial
CM
Christophe Massard, MD
Specialist
PI on 1 active trial
IP
Isabelle Ray-Coquard, Physician
Specialist
PI on 1 active trial

Treatment Centers

8 centers
⚗️ Trial Site

Washington University School of Medicine

📍 St Louis, Missouri

👤 Meagan A Jacoby, M.D., Ph.D.

👤 Janssen Research & Development, LLC Clinical Trial

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

Financial Resources

2 resources
Lynparza(olaparib)AstraZeneca Pharmaceuticals LP
Zejula(niraparib)GlaxoSmithKline, LLC.

Travel Grants

No travel grants are currently matched to Rare ovarian cancer.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Rare ovarian cancer

1 articles
NewsAMERICAN JOURNAL OF OBSTETRICS AND GYNECOLOGYMar 12, 2026
Endometrial pathology and surgical extent in ovarian adult granulosa cell tumor: associations with stage and survival.
Adult granulosa cell tumor is a rare ovarian cancer with less aggressive behavior than epithelial ovarian cancer. However, recurrence occurs in up to 30% of pat
See all news about Rare ovarian cancer

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Rare ovarian cancer

What is Rare ovarian cancer?

Rare ovarian cancer encompasses a heterogeneous group of uncommon malignant tumors arising from the ovary that do not fall into the category of common epithelial ovarian carcinomas (such as high-grade serous carcinoma). This broad category includes several distinct histological subtypes such as small cell carcinoma of the ovary (hypercalcemic type), ovarian clear cell carcinoma, low-grade serous carcinoma, mucinous ovarian carcinoma, granulosa cell tumors, Sertoli-Leydig cell tumors, ovarian carcinosarcoma, and other rare subtypes. Each subtype has distinct molecular, clinical, and prognostic

How is Rare ovarian cancer inherited?

Rare ovarian cancer follows a multifactorial inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

Are there clinical trials for Rare ovarian cancer?

Yes — 1 recruiting clinical trial is currently listed for Rare ovarian cancer on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.

Which specialists treat Rare ovarian cancer?

9 specialists and care centers treating Rare ovarian cancer are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Rare ovarian cancer?

4 patient support programs are currently tracked on UniteRare for Rare ovarian cancer. See the treatments and support programs sections for copay assistance, eligibility, and contact details.