Clinical trials for Phenylketonuria
19 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGPhase 3NCT06971731A Study to Evaluate the Safety and Efficacy of JNT-517 in Participants With Phenylketonuria (PKU)Otsuka Pharmaceutical Development & Commercialization, Inc. · PI: Otsuka Call Center
- ACTIVE NOT RECRUITINGPhase 1NCT07255599Evaluation of BH4 Responsiveness in Our PKU PatientsSohag University
- RECRUITINGN/ANCT06941532GMP Powdered Substitutes in PKU and TYRNutricia UK Ltd · PI: Gary Hubbard, Dr
- ENROLLING BY INVITATIONN/ANCT06940193A Self-test Home-use Blood Phenylalanine Monitoring System Under the Brand Name Egoo Phe System Has Been Developed for Measurement of Phenylalanine (Phe) in Individuals Diagnosed With Phenylketonuria (PKU): The Study Purpose is to Evaluate Accuracy and UsabilityEgoo Health Aps · PI: Anita MacDonald
- ACTIVE NOT RECRUITINGPhase 4NCT06901323Effect of L-carnitine Supplementation on Phenylalanine and Brain-derived Neurotrophic Factor Levels in Infants and Children With PhenylketonuriaMansoura University
- RECRUITINGN/ANCT06969209Brain Aging in PhenylketonuriaInsel Gruppe AG, University Hospital Bern · PI: Regula Everts, Prof. Dr. phil.
- RECRUITINGPhase 1NCT06332807AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)NGGT INC. · PI: Study Contact
- RECRUITINGN/ANCT06560736Development of Novel Psychological Assessment Tools and Anxiety Intervention for PhenylketonuriaUniversity of Missouri-Columbia · PI: Shawn Christ
- RECRUITINGN/ANCT06718842Walking Program in Fatty Liver Children With PhenylketonuriaCairo University · PI: Ali Ismail, lecturer
- RECRUITINGPhase 1NCT06687733Safety and Efficacy Study of NGGT002 in cPKU Adult SubjectsNGGT (Suzhou) Biotechnology Co., Ltd. · PI: Jianping Weng, PhD
- RECRUITINGPhase 3NCT06302348A Study of Sepiapterin in Participants With Phenylketonuria (PKU)PTC Therapeutics · PI: Patient Advocacy
- RECRUITINGN/ANCT06305234A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)BioMarin Pharmaceutical · PI: Medical Director, MD
- ACTIVE NOT RECRUITINGPhase 1NCT05972629A Phase 1/Phase 2 Open-label Study to Evaluate the Safety, Tolerability, and Efficacy of a Single Intravenous Administration of SAR444836 in Adult Participants With PhenylketonuriaSanofi · PI: Clinical Sciences & Operations
- RECRUITINGEarly Phase 1NCT06061614Safety and Efficacy Study of NGGT002 in PKU Adult SubjectsThe First Affiliated Hospital of Bengbu Medical University · PI: Huan Zhou, Doctor
- ACTIVE NOT RECRUITINGPhase 3NCT05270837Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With PhenylketonuriaBioMarin Pharmaceutical · PI: Study Director
- RECRUITINGN/ANCT05813678A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)BioMarin Pharmaceutical · PI: Medical Director, MD
- ACTIVE NOT RECRUITINGPhase 3NCT05166161A Long-Term Safety Study of PTC923 in Participants With PhenylketonuriaPTC Therapeutics
- RECRUITINGN/ANCT05128149Metabolic Control and Patient Well-being in Phenylketonuria: do Guidelines Make a Difference?University Children's Hospital, Zurich · PI: Martina Huemer, Prof
- ENROLLING BY INVITATIONN/ANCT04348708Long-Term Follow Up Study of Subjects Previously Administered HMI 102Homology Medicines, Inc