Active, not recruitingPhase 3NCT05166161
A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria
Studying Phenylketonuria
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- PTC Therapeutics
- Intervention
- PTC923(drug)
- Enrollment
- 200 enrolled
- Eligibility
- All sexes
- Timeline
- 2022 – 2026
Study locations (20)
- Children's Hospital Colorado, Aurora, Colorado, United States
- UF College of Medicine, Department of Pediatrics Division of Genetics and Metabolism, Gainesville, Florida, United States
- Indiana University School of Medicine Department of Medical and Molecular Genetics, Indianapolis, Indiana, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- Icahn School of Medicine at Mount Sinai (ISMMS), New York, New York, United States
- UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
- University of Utah, Salt Lake City, Utah, United States
- Westmead Hospital, Westmead, New South Wales, Australia
- PARC Clinical Research, Adelaide, South Australia, Australia
- Royal Children's Hospital, Parkville, Victoria, Australia
- Hospital de clinicas de Porto Alegre, Porto Alegre, Rio Grande do Sul, Brazil
- Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto da Universidade de São Paulo, Ribeirão Preto, São Paulo, Brazil
- Metabolics and Genetics in Calgary (MAGIC) Clinic, Ltd., Calgary, Alberta, Canada
- McMaster Children's Hospital Hamilton Health Sciences, Hamilton, Ontario, Canada
- The Hospital for Sick Children University of Toronto Adult Clinic: The Fred A Litwin Family Centre in Genetic Medicine University Health Network & Mt. Sinai Hospital, Toronto, Ontario, Canada
- +5 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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