Treatments for Phenylketonuria

FDA-approved drugs, patient assistance programs, and travel grants tracked on UniteRare for this condition.

Treatment data is extracted from FDA drug labels, DailyMed, and openFDA through automated and AI-assisted pipelines that read both structured records and unstructured label text.
Report missing data

FDA-approved treatments (4)

Patient support programs (9)

Copay cards, manufacturer assistance, and foundation grants. Verification status shown on each card.

Good Days — Phenylketonuria

Good Days

Phenylketonuria

Verified 17d ago
Foundation Grant
foundation grant
Accepting applications
Apply

Patient Services Inc — Phenylketonuria

Patient Services Inc

Phenylketonuria

Verified 17d ago
Foundation Grant
foundation grant
Accepting applications
Apply

PAN Foundation — Phenylketonuria

PAN Foundation

Phenylketonuria

Verified 17d ago
Foundation Grant
foundation grant
Currently closed
Apply Get notified when open

NORD Patient Assistance — Phenylketonuria

NORD Patient Assistance

Phenylketonuria

Verified 17d ago
Foundation Grant
foundation grant
Accepting applications
Apply

HealthWell Foundation — Phenylketonuria

HealthWell Foundation

Phenylketonuria

Verified 17d ago
Foundation Grant
foundation grant
Accepting applications
Apply

The Assistance Fund — Phenylketonuria

The Assistance Fund

Phenylketonuria

Verified 17d ago
Foundation Grant
foundation grant
Accepting applications
Apply

SAPROPTERIN DIHYDROCHLORIDE

BioMarin

Phenylketonuria

Unverified — confirm before calling
copay card
Copay CardPatient Assistance
Accepting applications
1-866-906-6100

Palynziq

BioMarin

Phenylketonuria

Unverified — confirm before calling
copay card
Copay CardPatient Assistance
Accepting applications
1-866-906-6100

Kuvan

BioMarin

Phenylketonuria

Unverified — confirm before calling
copay card
Copay CardPatient Assistance
Accepting applications
1-866-906-6100

More about Phenylketonuria