Perivascular epithelioid cell neoplasm

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ORPHA:595133D21.9
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4FDA treatments37Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Also known as:

Perivascular epithelioid tumourPEComa
Orphanet ↗NORD ↗

FDA & Trial Timeline

1 event
Nov 2021

Fyarro: FDA approved

treatment of adult patients with locally advanced unresectable or metastatic malignant perivascular epithelioid cell tumor (PEComa)

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

4 available

Urea 39.5% With 2% Salicylic Acid

UREA, SALICYLIC ACID· PureTek Corporation

Urea is useful for the treatment of hyperkeratotic conditions such as eczema

View Details →FDA Label ↗

Dermacure

UREA 41%· Oncora Pharma, LLC

Urea is useful for the treatment of hyperkeratotic conditions such as eczema

View Details →FDA Label ↗

Urea Cream 40 Percent

UREA· Method Pharmaceuticals, LLC

Urea is useful for the treatment of hyperkeratotic conditions such as eczema

View Details →FDA Label ↗

Fyarro

sirolimus protein-bound particles for injectable suspension (albumin-bound)· Aadi Bioscience, Inc.Orphan Drug

treatment of adult patients with locally advanced unresectable or metastatic malignant perivascular epithelioid cell tumor (PEComa)

View Details →FDA Label ↗

Clinical Trials

View all trials with filters →

No actively recruiting trials found for Perivascular epithelioid cell neoplasm at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Perivascular epithelioid cell neoplasm community →

Specialists

Showing 25 of 37View all specialists →
FM
Francis X McCormack, MD
STURGEON BAY, WI
Specialist
PI on 3 active trials
SM
Sergio A Harari, MD
Specialist
PI on 1 active trial
DP
David J Kwiatkowski, MD PhD
Specialist
PI on 1 active trial
MM
Michael Darcy, MD
OXNARD, CA
Specialist
PI on 1 active trial
TM
Timothy S Blackwell, MD
Specialist
PI on 1 active trial
CP
Carlos RR Carvalho, PhD
Specialist
PI on 1 active trial
MM
Mariana S Araujo, MD
DUBLIN, OH
Specialist
PI on 1 active trial
TB
Tim Brits
Specialist
1 Perivascular epithelioid cell neoplasm publication
JJ
Junjun Jia
Specialist
1 Perivascular epithelioid cell neoplasm publication
GG
Guomei Ge
Specialist
1 Perivascular epithelioid cell neoplasm publication
MF
Meibao Feng
Specialist
1 Perivascular epithelioid cell neoplasm publication
LL
Li Liu
Specialist
1 Perivascular epithelioid cell neoplasm publication
SZ
Shusen Zheng
Specialist
1 Perivascular epithelioid cell neoplasm publication
SW
Stefan De Wachter
NEW ULM, MN
Specialist
1 Perivascular epithelioid cell neoplasm publication
JY
Jun Yu
NASHUA, NH
Specialist
1 Perivascular epithelioid cell neoplasm publication
TB
Tokuro Baba
Specialist
1 Perivascular epithelioid cell neoplasm publication
BL
Binglin Lai
Specialist
1 Perivascular epithelioid cell neoplasm publication
ZA
Zeno Adriaenssens
Specialist
1 Perivascular epithelioid cell neoplasm publication
RL
Robby Peter Anna Lamoury
Specialist
1 Perivascular epithelioid cell neoplasm publication
ST
Sam Tilborghs
Specialist
1 Perivascular epithelioid cell neoplasm publication
JM
Joel Moss, M.D.
Bethesda, Maryland
Specialist

Rare Disease Specialist

PI on 11 active trials
WM
Willis Navarro, MD
TUCSON, AZ
Specialist
PI on 4 active trials
SP
Sandip P Patel
Birmingham, Alabama
Specialist

Rare Disease Specialist

PI on 1 active trial
AW
Aaron R Weiss
Specialist
PI on 1 active trial56 Perivascular epithelioid cell neoplasm publications
RM
Robert Maki, MD, MPH
PHILADELPHIA, PA
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center ↗

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center ↗

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program ↗

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site ↗

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site ↗

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site ↗

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine ↗

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program ↗

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Perivascular epithelioid cell neoplasm.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Perivascular epithelioid cell neoplasmForum →

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Latest news about Perivascular epithelioid cell neoplasm

2 articles
NewsMODERN PATHOLOGY : AN OFFICIAL JOURNAL OF THE UNITED STATES AND CANADIAN ACADEMY OF PATHOLOGY, INCMar 20, 2026
Alternative Lengthening of Telomeres in Malignant Perivascular Epithelioid Cell Neoplasms: Correlation With Molecular Features Including ATRX Gene Mutation Status.
A subset of perivascular epithelioid cell neoplasms (PEComas) is histologically malignant and at high risk for metastasis, and there is limited literature avail…
NewsUROLOGIC ONCOLOGYJan 18, 2026
Renal epithelioid angiomyolipoma: A multi-institutional, international cohort study with emphasis on clinicopathologic prognostic indicators.
Renal angiomyolipoma (AML) is a benign perivascular epithelioid cell neoplasm that is often associated with tuberous sclerosis complex (TSC). Epithelioid AML (e…
See all news about Perivascular epithelioid cell neoplasm →

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Perivascular epithelioid cell neoplasm

Which specialists treat Perivascular epithelioid cell neoplasm?

25 specialists and care centers treating Perivascular epithelioid cell neoplasm are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.