Ocular albinism

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:284804
Who is this for?
Show terms as
25Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Ocular albinism is a genetic condition that mainly affects the eyes, causing reduced pigment (color) in the iris and retina. Unlike other forms of albinism that affect the skin and hair, people with ocular albinism usually have normal or near-normal skin and hair coloring. The condition is also sometimes called ocular albinism type 1 (OA1) or Nettleship-Falls ocular albinism. The main symptoms involve vision problems. People with ocular albinism typically have reduced visual sharpness (visual acuity), involuntary eye movements called nystagmus, and sensitivity to bright light (photophobia). The iris may appear translucent or lighter than expected, and the retina at the back of the eye lacks its normal pigmentation. Many individuals also have problems with depth perception and may have crossed eyes (strabismus). These vision issues occur because the lack of pigment in the retina disrupts normal development of the nerve connections between the eyes and the brain. There is currently no cure for ocular albinism, and treatment focuses on managing vision problems. Corrective lenses, tinted glasses or contact lenses to reduce light sensitivity, and sometimes surgery for strabismus can help improve quality of life. Low-vision aids and educational accommodations are also important, especially for children. With proper support, most people with ocular albinism lead full and active lives.

Key symptoms:

Reduced vision or poor visual sharpnessInvoluntary rapid eye movements (nystagmus)Sensitivity to bright light (photophobia)Reduced pigment in the iris, making it appear translucentReduced pigment in the retinaCrossed eyes or misaligned eyes (strabismus)Poor depth perceptionDifficulty seeing fine detailsAbnormal routing of nerve signals from the eyes to the brainFoveal hypoplasia (underdeveloped central part of the retina)Color vision that is usually normal or mildly affected

Inheritance

X-linked recessive

Carried on the X chromosome; typically affects males more than females

Age of Onset

Infantile

Begins in infancy, roughly 1 month to 2 years old

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Ocular albinism.

View clinical trials →

No actively recruiting trials found for Ocular albinism at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Ocular albinism community →

Specialists

25 foundView all specialists →
LM
Lisa R. Young, MD
Specialist
PI on 1 active trial1 Ocular albinism publication
FD
Fanny MORICE-PICARD, Dr
Specialist
PI on 1 active trial
OP
Olivier Lortholary, MD, PhD
Specialist
PI on 5 active trials
WM
Wendy J Introne, M.D.
Bethesda, Maryland
Specialist

Rare Disease Specialist

PI on 4 active trials
BM
Brian P Brooks, M.D.
Bethesda, Maryland
Specialist

Rare Disease Specialist

PI on 8 active trials
CM
Christen Ebens, MD
MINNEAPOLIS, MN
Specialist
PI on 2 active trials
AP
Antoni Gostynski, MD, PhD
Maastricht, Limburg
Specialist

Rare Disease Specialist

PI on 2 active trials
SP
Smail HADJ-RABIA, MD, PhD
Specialist
PI on 1 active trial
GM
Guillemette FOUQUET, MD
Specialist
PI on 1 active trial1 Ocular albinism publication
MP
Menno A. De Rie, MD, PhD
Specialist
PI on 1 active trial
KC
Kevin J O'Brien, C.R.N.P.
Specialist
PI on 1 active trial
AP
Albert Wolkerstorfer, MD, PhD
Specialist
PI on 1 active trial
DM
David R Adams, M.D.
Specialist
PI on 1 active trial
MF
Mary E. Frey
Specialist
PI on 1 active trial18 Ocular albinism publications
SP
Sameek Roychowdhury, MD, PhD
COLUMBUS, OH
Specialist
PI on 2 active trials
JM
Joshua D. Milner, MD
NEW YORK, NY
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Ocular albinism.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Ocular albinismForum →

No community posts yet. Be the first to share your experience with Ocular albinism.

Start the conversation →

Latest news about Ocular albinism

No recent news articles for Ocular albinism.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What is my child's current level of visual acuity, and is it expected to change over time?,What low-vision aids or assistive devices would you recommend for school or daily activities?,Should we pursue genetic testing to confirm the diagnosis and identify the specific mutation?,Are there any clinical trials or emerging treatments for ocular albinism?,What school accommodations should we request for our child?,Is surgery recommended for the strabismus, and what are the expected outcomes?,What are the chances of passing this condition to future children, and should other family members be tested?

Common questions about Ocular albinism

What is Ocular albinism?

Ocular albinism is a genetic condition that mainly affects the eyes, causing reduced pigment (color) in the iris and retina. Unlike other forms of albinism that affect the skin and hair, people with ocular albinism usually have normal or near-normal skin and hair coloring. The condition is also sometimes called ocular albinism type 1 (OA1) or Nettleship-Falls ocular albinism. The main symptoms involve vision problems. People with ocular albinism typically have reduced visual sharpness (visual acuity), involuntary eye movements called nystagmus, and sensitivity to bright light (photophobia). T

How is Ocular albinism inherited?

Ocular albinism follows a x-linked recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Ocular albinism typically begin?

Typical onset of Ocular albinism is infantile. Age of onset can vary across affected individuals.

Which specialists treat Ocular albinism?

25 specialists and care centers treating Ocular albinism are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.