Non-severe combined immunodeficiency

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16Specialists8Treatment centers1Financial resources

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Overview

Non-severe combined immunodeficiency (non-severe CID) is a rare immune system disorder where the body's defense system does not work properly, but is not completely absent as in the most serious form called severe combined immunodeficiency (SCID). In this condition, both the T cells and B cells — the white blood cells that fight infections — are reduced in number or do not function as well as they should. However, enough immune function remains that affected individuals may survive longer without treatment compared to those with SCID. People with non-severe CID are much more vulnerable to infections than healthy individuals. They may get sick more often, have infections that are harder to treat, or develop infections caused by germs that would not normally make a healthy person ill (called opportunistic infections). Common problems include repeated lung infections, chronic diarrhea, skin infections, and infections caused by viruses like cytomegalovirus (CMV) or fungi like Candida. Some people also have autoimmune problems, where the immune system mistakenly attacks the body's own tissues. Treatment depends on the specific cause and severity. Options may include immunoglobulin replacement therapy (giving antibodies through an IV or under the skin), preventive antibiotics or antifungals, and in some cases, a bone marrow or stem cell transplant. Early diagnosis and treatment are very important to prevent serious complications and improve quality of life.

Also known as:

Key symptoms:

Frequent or repeated infections (ear, lung, sinus, skin)Infections that are unusually severe or hard to treatInfections caused by unusual germs (opportunistic infections)Chronic diarrhea or stomach problemsSlow growth or failure to gain weight in childrenPersistent thrush (yeast infection in the mouth)Skin rashes or eczemaSwollen lymph nodes or enlarged spleenAutoimmune problems (immune system attacking own body)Fatigue and low energyRecurrent pneumonia or bronchitis

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Non-severe combined immunodeficiency.

View clinical trials →

No actively recruiting trials found for Non-severe combined immunodeficiency at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Non-severe combined immunodeficiency community →

Specialists

16 foundView all specialists →
PM
Paul Szabolcs, MD
Pittsburgh, Pennsylvania
Specialist

Rare Disease Specialist

PI on 7 active trials
MM
Mitchell S Cairo, MD
HAWTHORNE, NY
Specialist
PI on 12 active trials
AM
Amrita Y. Krishnan, MD
DUARTE, CA
Specialist
PI on 4 active trials1 Non-severe combined immunodeficiency publication
BM
Biljana Horn, MD
SAN FRANCISCO, CA
Specialist
PI on 2 active trials
JR
Juan C Ramos
Specialist
PI on 1 active trial37 Non-severe combined immunodeficiency publications
SM
Suhag Parikh, MD
CHICAGO, IL
Specialist
PI on 1 active trial
CM
Christen Ebens, MD
MINNEAPOLIS, MN
Specialist
PI on 2 active trials
AW
Ann Woolfrey
SEATTLE, WA
Specialist
PI on 5 active trials
AP
Alessandra MAGNANI, MD, PhD
LONG BEACH, CA
Specialist
PI on 1 active trial
JP
James Garvin, MD, PhD
Specialist
PI on 1 active trial
FM
Farheen Quadri, MBBS, MSCR
Specialist
PI on 1 active trial
AF
Ali F Saleem, MBBS, MCR, FCPS
NEW HYDE PARK, NY
Specialist
PI on 1 active trial
AS
Anita K.M Zaidi, MBBS, SM
NEW YORK, NY
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Financial Resources

1 resources

Revcovi

Chiesi USA Inc.

Revcovi Patient Support (Chiesi Patient Support)

Patient Assistance
Manufacturer Program
Accepting applications

Travel Grants

No travel grants are currently matched to Non-severe combined immunodeficiency.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Non-severe combined immunodeficiencyForum →

No community posts yet. Be the first to share your experience with Non-severe combined immunodeficiency.

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Latest news about Non-severe combined immunodeficiency

No recent news articles for Non-severe combined immunodeficiency.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Which specific gene is causing my (or my child's) immune deficiency, and what does that mean for treatment options?,Do I need immunoglobulin replacement therapy, and if so, which type and how often?,Should I consider a stem cell transplant, and am I (or is my child) a good candidate?,Which vaccines are safe for me (or my child) to receive?,What infections should I watch for most closely, and when should I go to the emergency room?,Are there any clinical trials or gene therapy options I should know about?,Should other family members be tested for this condition?

Common questions about Non-severe combined immunodeficiency

What is Non-severe combined immunodeficiency?

Non-severe combined immunodeficiency (non-severe CID) is a rare immune system disorder where the body's defense system does not work properly, but is not completely absent as in the most serious form called severe combined immunodeficiency (SCID). In this condition, both the T cells and B cells — the white blood cells that fight infections — are reduced in number or do not function as well as they should. However, enough immune function remains that affected individuals may survive longer without treatment compared to those with SCID. People with non-severe CID are much more vulnerable to inf

Which specialists treat Non-severe combined immunodeficiency?

16 specialists and care centers treating Non-severe combined immunodeficiency are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for Non-severe combined immunodeficiency?

1 patient support program are currently tracked on UniteRare for Non-severe combined immunodeficiency. See the treatments and support programs sections for copay assistance, eligibility, and contact details.