Neurocutaneous syndrome with epilepsy

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ORPHA:166466
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8Specialists8Treatment centers

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Overview

Neurocutaneous syndrome with epilepsy is an extremely rare condition that belongs to a group of disorders known as neurocutaneous syndromes (also sometimes called phakomatoses). These are conditions that affect both the skin and the nervous system at the same time. In this particular syndrome, patients develop skin abnormalities alongside seizures (epilepsy) as a core feature. The skin findings may include unusual birthmarks, patches of differently colored skin, or other visible changes. The epilepsy component means that the brain has abnormal electrical activity that leads to repeated seizures, which can vary in type and severity from person to person. Because this is such a rare condition, detailed information about its full range of symptoms, underlying genetic cause, and best treatment approaches is limited. Treatment is generally focused on managing symptoms, particularly controlling seizures with anti-epileptic medications and addressing any skin-related concerns. A team of specialists including neurologists and dermatologists typically works together to provide care. Some patients may also experience developmental delays or learning difficulties, though the severity can vary widely. Early diagnosis and seizure management are important for improving quality of life and developmental outcomes.

Key symptoms:

Seizures or epilepsySkin abnormalities such as unusual birthmarks or pigment changesDevelopmental delaysLearning difficultiesIntellectual disability in some casesAbnormal skin patches or lesionsPossible behavioral challengesPossible vision problemsPossible movement difficulties

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Neurocutaneous syndrome with epilepsy.

View clinical trials →

No actively recruiting trials found for Neurocutaneous syndrome with epilepsy at this time.

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Search ClinicalTrials.gov ↗Join the Neurocutaneous syndrome with epilepsy community →

Specialists

8 foundView all specialists →
EM
Eric H Kossoff, MD
BALTIMORE, MD
Specialist
PI on 6 active trials
MM
Martina Bebin, MD, MPA
Specialist
PI on 2 active trials
KK
Katarzyna Kotulska-Jozwiak
Specialist
PI on 1 active trial2 Neurocutaneous syndrome with epilepsy publications
DM
Dennis J Dlugos, MD
PHILADELPHIA, PA
Specialist
PI on 2 active trials
AP
Anna Jansen, MD, PhD
Silver Spring, Maryland
Specialist

Rare Disease Specialist

PI on 2 active trials
DP
Darcy Krueger, M.D. Ph.D
CINCINNATI, OH
Specialist
PI on 1 active trial
RP
Rima Nabbout, MD, PhD
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Neurocutaneous syndrome with epilepsy.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Neurocutaneous syndrome with epilepsy

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What type of seizures does my child have, and what is the best medication to control them?,Are there any genetic tests that could help identify the exact cause of this condition?,What should I do if a seizure lasts longer than 5 minutes?,How often should we have follow-up brain imaging or EEG testing?,Are there any clinical trials or research studies we could participate in?,What developmental therapies would benefit my child the most?,Could this condition be passed on to future children?

Common questions about Neurocutaneous syndrome with epilepsy

What is Neurocutaneous syndrome with epilepsy?

Neurocutaneous syndrome with epilepsy is an extremely rare condition that belongs to a group of disorders known as neurocutaneous syndromes (also sometimes called phakomatoses). These are conditions that affect both the skin and the nervous system at the same time. In this particular syndrome, patients develop skin abnormalities alongside seizures (epilepsy) as a core feature. The skin findings may include unusual birthmarks, patches of differently colored skin, or other visible changes. The epilepsy component means that the brain has abnormal electrical activity that leads to repeated seizure

Which specialists treat Neurocutaneous syndrome with epilepsy?

8 specialists and care centers treating Neurocutaneous syndrome with epilepsy are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.