Neonatal dermatomyositis

Last reviewed

🖨 Print for my doctorAdvocacy Hub →
ORPHA:398117M33.1
Who is this for?
Show terms as
3Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
Report missing data

Overview

Neonatal dermatomyositis is an extremely rare inflammatory condition that appears in newborns, combining features of skin inflammation (dermato-) and muscle inflammation (myositis). It belongs to the broader group of inflammatory myopathies, which are conditions where the body's immune system mistakenly attacks its own muscles and skin. In this neonatal form, symptoms are present at birth or develop within the first weeks of life, which is very unusual since dermatomyositis typically affects older children or adults. Babies with this condition may show characteristic skin rashes, including a purplish or reddish discoloration around the eyes (called a heliotrope rash) and reddened patches over the knuckles, elbows, or knees (called Gottron papules). Muscle weakness is another hallmark, which can make the baby appear floppy or have difficulty feeding and moving. In some cases, the condition may also affect internal organs, including the lungs and heart. Because this condition is so rare, there is no single established treatment protocol. Management typically involves immunosuppressive medications such as corticosteroids and other drugs that calm the overactive immune system. Supportive care, including physical therapy and nutritional support, plays an important role. The treatment approach is largely borrowed from what is known about juvenile dermatomyositis, adapted for the unique needs of a newborn. Early diagnosis and aggressive treatment are important to prevent complications and improve outcomes.

Also known as:

Key symptoms:

Skin rash with purplish discoloration around the eyesRed or purple patches over the knuckles, elbows, or kneesMuscle weakness or floppinessDifficulty feeding or swallowingPoor muscle tone (baby feels limp)Skin thickening or hardeningCalcium deposits under the skinFatigue and low energyDifficulty breathingJoint stiffness or contracturesFailure to thrive or poor weight gainIrritability or excessive crying

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Neonatal dermatomyositis.

View clinical trials →

No actively recruiting trials found for Neonatal dermatomyositis at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Neonatal dermatomyositis community →

Specialists

3 foundView all specialists →
MM
Monique Hinchcliff, MD
NORTH HAVEN, CT
Specialist
PI on 2 active trials
AM
Adela Cardones, MD
DURHAM, NC
Specialist
PI on 2 active trials

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Neonatal dermatomyositis.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Neonatal dermatomyositisForum →

No community posts yet. Be the first to share your experience with Neonatal dermatomyositis.

Start the conversation →

Latest news about Neonatal dermatomyositis

No recent news articles for Neonatal dermatomyositis.

Follow this condition to be notified when news becomes available.

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What is the severity of my baby's condition, and what organs are affected?,What treatment plan do you recommend, and what are the potential side effects?,How will we monitor my baby's response to treatment?,What signs of complications should I watch for at home?,Will my baby need physical therapy, and how often?,Are there any clinical trials or new treatments being studied for this condition?,What is the expected long-term outlook for my child's development and quality of life?

Common questions about Neonatal dermatomyositis

What is Neonatal dermatomyositis?

Neonatal dermatomyositis is an extremely rare inflammatory condition that appears in newborns, combining features of skin inflammation (dermato-) and muscle inflammation (myositis). It belongs to the broader group of inflammatory myopathies, which are conditions where the body's immune system mistakenly attacks its own muscles and skin. In this neonatal form, symptoms are present at birth or develop within the first weeks of life, which is very unusual since dermatomyositis typically affects older children or adults. Babies with this condition may show characteristic skin rashes, including a

At what age does Neonatal dermatomyositis typically begin?

Typical onset of Neonatal dermatomyositis is neonatal. Age of onset can vary across affected individuals.

Which specialists treat Neonatal dermatomyositis?

3 specialists and care centers treating Neonatal dermatomyositis are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.