Overview
Hurler Syndrome is treated with 1 medication in our database, including ALDURAZYME. 1 of these has manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Sanofi. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Hurler Syndrome treatment below.
Clinical phenotype terms— hover any for plain English:
FDA & Trial Timeline
1 eventOrchard Therapeutics — PHASE3
Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
Treatments
1 availableALDURAZYME
Patients with Hurler and Hurler-Scheie forms of Mucopolysaccharidosis I (MPS I) and patients with the Scheie form who have moderate to severe symptoms. Reduces urinary glycosaminoglycans and improves …
Patients with Hurler and Hurler-Scheie forms of Mucopolysaccharidosis I (MPS I) and patients with the Scheie form who have moderate to severe symptoms. Reduces urinary glycosaminoglycans and improves walking capacity and pulmonary function.
Rare Disease Specialist
Treatment Centers
8 centersBaylor College of Medicine Rare Disease Center ↗
Baylor College of Medicine
📍 Houston, TX
🏥 NORDStanford Medicine Rare Disease Center ↗
Stanford Medicine
📍 Stanford, CA
🔬 UDNNIH Clinical Center Undiagnosed Diseases Program ↗
National Institutes of Health
📍 Bethesda, MD
🔬 UDNUCLA UDN Clinical Site ↗
UCLA Health
📍 Los Angeles, CA
🔬 UDNBaylor College of Medicine UDN Clinical Site ↗
Baylor College of Medicine
📍 Houston, TX
🔬 UDNHarvard/MGH UDN Clinical Site ↗
Massachusetts General Hospital
📍 Boston, MA
🏥 NORDMayo Clinic Center for Individualized Medicine ↗
Mayo Clinic
📍 Rochester, MN
👤 Mayo Clinic Center for Individualized Medicine
🏥 NORDUCLA Rare Disease Day Program ↗
UCLA Health
📍 Los Angeles, CA
Financial Resources
1 resources1 travel grant are also available for Hurler syndrome patients — see Travel Grants below ↓
Travel Grants
1 grantsAldurazyme Co-Pay Assistance Program
Community
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Caregiver Resources
NORD Caregiver Resources
Support, advocacy, and financial assistance for caregivers of rare disease patients.
Mental Health Support
Rare disease caregiving can be isolating. Connect with counseling and peer support.
Family & Caregiver Grants
Financial assistance programs specifically for caregivers of rare disease patients.
Social Security Disability
Learn how rare disease patients may qualify for SSDI/SSI benefits.
Common questions about Hurler syndrome
What is Hurler syndrome?
Hurler Syndrome is treated with 1 medication in our database, including ALDURAZYME. 1 of these has manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Sanofi. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Hurler Syndrome treatment below.
Are there clinical trials for Hurler syndrome?
Yes — 1 recruiting clinical trial is currently listed for Hurler syndrome on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.
Which specialists treat Hurler syndrome?
18 specialists and care centers treating Hurler syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.
What treatment and support options exist for Hurler syndrome?
1 FDA-approved treatment and 1 patient support program are currently tracked on UniteRare for Hurler syndrome. See the treatments and support programs sections for copay assistance, eligibility, and contact details.