Hurler-Scheie syndrome

Last reviewed

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ORPHA:93476OMIM:607015E76.0
Who is this for?
Show terms as
1FDA treatments10Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Also known as:

Clinical phenotype terms— hover any for plain English:

Spinal canal stenosisHP:0003416RhinitisHP:0012384Abnormal nerve conduction velocityHP:0040129Abnormality of the tonsilsHP:0100765
Orphanet ↗OMIM ↗NORD ↗

Treatments

1 available

ALDURAZYME

LARONIDASE· Genzyme Corporation■ Boxed WarningOrphan Drug

Patients with Hurler and Hurler-Scheie forms of Mucopolysaccharidosis I (MPS I) and patients with the Scheie form who have moderate to severe symptoms.

No actively recruiting trials found for Hurler-Scheie syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Hurler-Scheie syndrome community →

Specialists

10 foundView all specialists →
PM
Patricia I Dickson, MD
Specialist
PI on 3 active trials
SO
Shigetoyo Oguri
Specialist
PI on 1 active trial
PP
Patrice Rioux, MD PhD
Specialist
PI on 3 active trials
AS
Ashley Schneider
Specialist
PI on 1 active trial
MM
Michael Msall, M.D.
CHICAGO, IL
Specialist
PI on 1 active trial
AM
Agnes Chen, MD
TORRANCE, CA
Specialist
PI on 1 active trial
PM
Patricia K. Duffner, M.D.
BUFFALO, NY
Specialist
PI on 1 active trial
CM
Chester B. Whitley, Ph.D., M.D.
LAS VEGAS, NV
Specialist
PI on 1 active trial
CP
Chester B. Whitley, M.D., Ph.D.
LAS VEGAS, NV
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Hurler-Scheie syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

Open Hurler-Scheie syndromeForum →

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Latest news about Hurler-Scheie syndrome

No recent news articles for Hurler-Scheie syndrome.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about Hurler-Scheie syndrome

Which specialists treat Hurler-Scheie syndrome?

10 specialists and care centers treating Hurler-Scheie syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.