Hurler syndrome

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At a Glance

Live from database

Regulatory Watchboard

1 event
Dec 2023A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCT

Orchard Therapeutics — PHASE3

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

2 programs

FINANCIAL LANDSCAPE SUMMARY

2

Total programs

1

Open now

1

Copay cards

1

Travel grants

Copay Assistance1

ALDURAZYME

Sanofi

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Travel Grants1

Aldurazyme Co-Pay Assistance Program

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Approved Treatments

1 FDA-approved

ALDURAZYME

(LARONIDASE)Orphan drug

Genzyme Corporation

FDA label ↗

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Clinical Trial Landscape

1 active trial
1Phase 3
1Total recruiting
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Recent News & Research

No recent news articles indexed yet for Hurler syndrome.
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Specialist Network

Top 6 by expertise

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