What is Duchenne or Becker Muscular Dystrophy?
Duchenne or Becker Muscular Dystrophy is treated with 2 medications in our database, including Viltepso, AMONDYS 45. 2 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Nippon Shinyaku, Sarepta. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Duchenne or Becker Muscular Dystrophy treatment below.
- Inheritance
- X-linked recessive
- Carried on the X chromosome; typically affects males more than females
- Age of Onset
- Childhood
- Begins in childhood, roughly ages 1 to 12
Treatments
2 availableSource: openFDA + DailyMed · NDA / BLA labels with structured indications · refreshed weekly
Viltepso
* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Not Publicly Available * RxBIN, PCN, and Group numbers: Not Publi
AMONDYS 45
* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Available only in the United States; patients must be pursuing or
Clinical Trials
View all trials with filters →Source: ClinicalTrials.gov · synced daily · phases, status, and PI names normalized at ingest
No actively recruiting trials found for Duchenne or Becker Muscular Dystrophy at this time.
New trials open frequently. Follow this disease to get notified.
Source: NPI Registry + PubMed · trial PI roles cross-referenced with ClinicalTrials.gov · ranked by match score (publications + PI activity + community signal)
Rare Disease Specialist
Treatment Centers
8 centersSource: NORD Rare Disease Centers + NIH Undiagnosed Diseases Network (UDN) · centers verified active within last 12 months
Children's Hospital Colorado Rare Disease Program ↗
Children's Hospital Colorado
📍 Aurora, CO
👤 Boston Children's Hospital Rare Disease Program
🔬 UDNHarvard/MGH UDN Clinical Site ↗
Massachusetts General Hospital
📍 Boston, MA
🏥 NORDBoston Children's Hospital Rare Disease Program ↗
Boston Children's Hospital
📍 Boston, MA
👤 Boston Children's Hospital Rare Disease Program
🏥 NORDUCLA Rare Disease Day Program ↗
UCLA Health
📍 Los Angeles, CA
🏨 Children'sAnn & Robert H. Lurie Children's Hospital Genetics ↗
Lurie Children's Hospital
📍 Chicago, IL
👤 Boston Children's Hospital Rare Disease Program
🏥 NORDCincinnati Children's Hospital Medical Center ↗
Cincinnati Children's
📍 Cincinnati, OH
👤 Boston Children's Hospital Rare Disease Program
🏨 Children'sNationwide Children's Hospital Rare Disease Center ↗
Nationwide Children's Hospital
📍 Columbus, OH
👤 Boston Children's Hospital Rare Disease Program
🔬 UDNNIH Clinical Center Undiagnosed Diseases Program ↗
National Institutes of Health
📍 Bethesda, MD
Travel Grants
1 grantsViltepso Access Programs (NS Support)
Eligible patients must be US residents under age 65 prescribed VILTEPSO for Duchenne muscular dystrophy. Financial assistance requires commercial insurance for the co-pay program or being uninsured with income at or below 400% of the Federal Poverty Level for the Patient Assistance Program.
Community
No community posts yet. Be the first to share your experience with Duchenne or Becker Muscular Dystrophy.
Start the conversation →Latest news about Duchenne or Becker Muscular Dystrophy
Source: PubMed + NIH RePORTER + openFDA + clinical-journal RSS · last 30 days · disease-tagged at ingest by AI extraction with human QC
No recent news articles for Duchenne or Becker Muscular Dystrophy.
Follow this condition to be notified when news becomes available.
Caregiver Resources
NORD Caregiver Resources
Support, advocacy, and financial assistance for caregivers of rare disease patients.
Mental Health Support
Rare disease caregiving can be isolating. Connect with counseling and peer support.
Family & Caregiver Grants
Financial assistance programs specifically for caregivers of rare disease patients.
Social Security Disability
Learn how rare disease patients may qualify for SSDI/SSI benefits.
Common questions about Duchenne or Becker Muscular Dystrophy
What is Duchenne or Becker Muscular Dystrophy?
Duchenne or Becker Muscular Dystrophy is treated with 2 medications in our database, including Viltepso, AMONDYS 45. 2 of these have manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Nippon Shinyaku, Sarepta. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Duchenne or Becker Muscular Dystrophy treatment below.
How is Duchenne or Becker Muscular Dystrophy inherited?
Duchenne or Becker Muscular Dystrophy follows a x-linked recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.
At what age does Duchenne or Becker Muscular Dystrophy typically begin?
Typical onset of Duchenne or Becker Muscular Dystrophy is childhood. Age of onset can vary across affected individuals.
Which specialists treat Duchenne or Becker Muscular Dystrophy?
1 specialists and care centers treating Duchenne or Becker Muscular Dystrophy are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.
What treatment and support options exist for Duchenne or Becker Muscular Dystrophy?
2 FDA-approved treatments and 1 patient support program are currently tracked on UniteRare for Duchenne or Becker Muscular Dystrophy. See the treatments and support programs sections for copay assistance, eligibility, and contact details.
Frequently asked questions about Duchenne or Becker Muscular Dystrophy
Auto-generated from canonical disease facts (Orphanet, OMIM, ClinicalTrials.gov, openFDA, NPPES). Not a substitute for clinical guidance.
What is Duchenne or Becker Muscular Dystrophy?
Duchenne or Becker Muscular Dystrophy is a rare disease catalogued in international rare-disease ontologies. It is typically inherited as x-linked recessive. Age of onset is generally childhood. For verified primary sources, see the UniteRare Duchenne or Becker Muscular Dystrophy page.
How is Duchenne or Becker Muscular Dystrophy inherited?
Duchenne or Becker Muscular Dystrophy follows x-linked recessive inheritance. Genetic counseling is recommended for affected families to understand recurrence risk in offspring and the likelihood of unaffected siblings being carriers. Variants in the underlying gene(s) may be identified via clinical genetic testing.
Are there FDA-approved treatments for Duchenne or Becker Muscular Dystrophy?
Yes — UniteRare tracks 2 FDA-approved treatments with indications relevant to Duchenne or Becker Muscular Dystrophy. Each entry includes prescribing information, orphan-drug-designation status where applicable, and the FDA application number for verification.
Are there clinical trials for Duchenne or Becker Muscular Dystrophy?
Active clinical trials for Duchenne or Becker Muscular Dystrophy are tracked daily from ClinicalTrials.gov. Trial availability changes frequently; check the UniteRare trial listings for the current count and recruitment status. Sponsors of rare-disease research often welcome inquiries even when a trial is not actively recruiting at a given moment.
How do I find a specialist for Duchenne or Becker Muscular Dystrophy?
UniteRare lists 1 verified clinician with documented expertise in Duchenne or Becker Muscular Dystrophy, sourced from ClinicalTrials.gov principal-investigator records, PubMed publication histories, and the NPPES NPI registry. Filter by state or browse our state-specific specialist pages for nearby options.
See full Duchenne or Becker Muscular Dystrophy page for complete clinical details, sources, and verified-specialist listings.
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