RecruitingPhase 2NCT07097311
Study to Evaluate the Use of Triheptanoin in Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD)
Studying Acyl-CoA dehydrogenase deficiency
Last synced from ClinicalTrials.gov
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Jerry Vockley, MD, PhD
- Principal Investigator
- Gerard Vockley, MD, PhDUPMC Children's Hospital of Pittsburgh
- Intervention
- Triheptanoin(drug)
- Enrollment
- 24 enrolled
- Eligibility
- 4 years · All sexes
- Timeline
- 2026 – 2028
Study locations (1)
- Children's Hospital of Pittsburgh of UPMC, Pittsburgh, Pennsylvania, United States
Collaborators
Ultragenyx Pharmaceutical Inc
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT07097311 on ClinicalTrials.govOther trials for Acyl-CoA dehydrogenase deficiency
Additional recruiting or active studies for the same condition.
- RECRUITINGPHASE2NCT06773026Study of Sodium Phenylbutyrate (ACER-001) for the Treatment of Pediatric and Adults Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD)Jerry Vockley, MD, PhD
- RECRUITINGNANCT06623032Metabolic Effects of Medium-Chain Fatty Acids in Patients With Medium-Chain Acyl-CoA Dehydrogenase Deficiency and Healthy IndividualsUniversity of Copenhagen