RecruitingPhase 2NCT06773026
Study of Sodium Phenylbutyrate (ACER-001) for the Treatment of Pediatric and Adults Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD)
Studying Acyl-CoA dehydrogenase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Jerry Vockley, MD, PhD
- Principal Investigator
- Gerard Vockley, MD, PhDUPMC Children's Hospital of Pittsburgh
- Intervention
- Sodium phenylbutyrate(drug)
- Enrollment
- 24 enrolled
- Eligibility
- 4 years · All sexes
- Timeline
- 2025 – 2027
Study locations (1)
- UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
Collaborators
Zevra Therapeutics
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT06773026 on ClinicalTrials.govOther trials for Acyl-CoA dehydrogenase deficiency
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- RECRUITINGNANCT06623032Metabolic Effects of Medium-Chain Fatty Acids in Patients With Medium-Chain Acyl-CoA Dehydrogenase Deficiency and Healthy IndividualsUniversity of Copenhagen