Active, not recruitingPhase 3NCT06455059
Interventional Study of Vosoritide for the Treatment of Children With Hypochondroplasia
Studying Hypochondroplasia
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- BioMarin Pharmaceutical
- Principal Investigator
- Medical Director, MD, MDBioMarin Pharmaceutical
- Intervention
- Vosoritide(drug)
- Enrollment
- 80 target
- Eligibility
- 3-17 years · All sexes
- Timeline
- 2024 – 2026
Study locations (23)
- Nemours Alfred I. DuPont Hospital for Children, Wilmington, Delaware, United States
- Children's National Medical Center, Washington D.C., District of Columbia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- Medical College of Wisconsin, Milwaukee, Wisconsin, United States
- Murdoch Children's Research Institute, Parkville, Victoria, Australia
- University of Alberta Stollery Children's Hospital, Edmonton, Alberta, Canada
- SickKids - The Hospital for Sick Children, Toronto, Ontario, Canada
- Centre Hospitalier Universitaire Sainte-Justine, Montreal, Quebec, Canada
- Hospices Civils de Lyon - Hopital Femme Mere Enfant, Lyon, France
- Hopital de la Timone, Marseille, France
- Hopital Necker-Enfants Malade, Paris, France
- CHU de Toulouse, Toulouse, France
- Uniklinik Koln, Cologne, Germany
- Univeristatskinderklinik Magdeburg, Magdeburg, Germany
- Instituto Giannina Gaslini, Genoa, Italy
- +8 more locations on ClinicalTrials.gov
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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