Clinical trials for Hypochondroplasia
7 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- ENROLLING BY INVITATIONPhase 2NCT07393373Open-Label, Long-Term, Extension Study of Infigratinib in Children With HypochondroplasiaQED Therapeutics, a BridgeBio company · PI: QED Therapeutics SVP, Clinical Development
- RECRUITINGPhase 2NCT07126262A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 MonthsBioMarin Pharmaceutical
- ENROLLING BY INVITATIONPhase 3NCT07073014Long-Term Extension Study of Vosoritide to Treat Children With HypochondroplasiaBioMarin Pharmaceutical
- ENROLLING BY INVITATIONPHASE2, PHASE3NCT06873035An Interventional Study of Infigratinib in Children With HypochondroplasiaQED Therapeutics, a BridgeBio company
- ACTIVE NOT RECRUITINGPhase 3NCT06455059Interventional Study of Vosoritide for the Treatment of Children With HypochondroplasiaBioMarin Pharmaceutical · PI: Medical Director, MD
- RECRUITINGNCT06410976Prospective Clinical Assessment Study in Children With HypochondroplasiaQED Therapeutics, a BridgeBio company
- RECRUITINGNCT06212947A Multicenter Multinational Observational Study of Children With HypochondroplasiaBioMarin Pharmaceutical · PI: Medical Director, MD