RecruitingPhase 1NCT06340685
Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) Deficiency
Studying Pyruvate dehydrogenase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Jirair Krikor Bedoyan
- Principal Investigator
- Jirair Bedoyan, MD, PhDUPMC Children's Hospital of Pittsburgh
- Intervention
- Triheptanoin(drug)
- Enrollment
- 6 enrolled
- Eligibility
- 1-17 years · All sexes
- Timeline
- 2024 – 2029
Study locations (1)
- UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, United States
Collaborators
Ultragenyx Pharmaceutical Inc
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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