Clinical trials for Pyruvate dehydrogenase deficiency
4 recruiting or active trials synced from ClinicalTrials.gov.
ℹ
Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGPhase 2NCT06887777Efficacy and Safety of the Treatment of Pyruvate Dehydrogenase Deficiency Patients With Glycerol Phenylbutyrate (RAVICTI)Assistance Publique - Hôpitaux de Paris
- RECRUITINGPhase 1NCT06340685Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) DeficiencyJirair Krikor Bedoyan · PI: Jirair Bedoyan, MD, PhD
- ACTIVE NOT RECRUITINGPhase 3NCT02616484Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency:Saol Therapeutics Inc · PI: Richard Neibeger, MD
- RECRUITINGNCT03056794Natural History and Advanced Genetic Study of Pyruvate Dehydrogenase Complex DeficienciesUniversity of Pittsburgh · PI: Jirair K. Bedoyan, MD, PhD