CompletedNCT05545774

Neuromuscular Characterisation in Late Adolescent and Adult Cystinosis Patients

Studying Cystinosis

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Key facts

Sponsor
Assistance Publique - Hôpitaux de Paris
Principal Investigator
Pascal Laforêt, MD, PhD
Neurology Department, Raymond Poincaré Hospital, APHP
Enrollment
20 enrolled
Eligibility
16 years · All sexes
Timeline
20222025

Study locations (2)

Collaborators

Cystinosis Research Foundation

Primary source

Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.

Open NCT05545774 on ClinicalTrials.gov

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