Clinical trials for Cystinosis
8 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGPHASE1, PHASE2NCT05994534PK and PD Study of NPI-001 and Cysteamine BitartrateNacuity Pharmaceuticals, Inc. · PI: Hugh McCarthy, PhD, FRACP
- RECRUITINGPHASE1, PHASE2NCT05508009Early Trial of Allogeneic Hematopoietic Stem Cell Transplantation for Patients Who Will Receive a Kidney Transplant From the Same DonorAlice Bertaina · PI: Alice Bertaina, MD
- ENROLLING BY INVITATIONN/ANCT05146830A Long-Term Follow-Up Study of Participants With Cystinosis Who Previously Received CTNS-RD-04Stephanie Cherqui · PI: Stephanie Cherqui, PhD
- RECRUITINGN/ANCT05959668Development of Health-related Quality of Life Instrument for Patients With CystinosisCystinose Stiftung · PI: Julia Hannah Quitmann, PD Dr.
- RECRUITINGN/ANCT05843851Genetic Newborn Screening for Cystinosis and Primary HyperoxaluriaCystinose Stiftung · PI: Sonja Froschauer
- ENROLLING BY INVITATIONNCT04246060Observational Study to Assess the Quality of Life in Nephropathic Cystinosis PatientsChiesi SA/NV
- RECRUITINGNCT05901077European Cystinosis CohortInstitut National de la Santé Et de la Recherche Médicale, France · PI: Aude Servais, PHD
- RECRUITINGN/ANCT00359684Use of Cysteamine in the Treatment of CystinosisNational Human Genome Research Institute (NHGRI) · PI: William A Gahl, M.D.