RecruitingPhase 3NCT05477563
Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
Studying Beta-thalassemia
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Vertex Pharmaceuticals Incorporated
- Intervention
- CTX001(biological)
- Enrollment
- 26 enrolled
- Eligibility
- 12-35 years · All sexes
- Timeline
- 2022 – 2027
Study locations (6)
- New York Presbyterian Hospital - Morgan Stanley Children's Hospital, New York, New York, United States
- Levine Children's Hospital - Hematology, Charlotte, North Carolina, United States
- TriStar Medical Group Children's Specialists - Pediatric Oncology, Nashville, Tennessee, United States
- University Hospital Dusseldorf - Department of Pediatric Oncology, Hematology and Clinical Immunology, Düsseldorf, Germany
- IRCSS Ospedale Pediatrico Bambino Gesu - Dipartimento di Onco-Ematologia e Terapia Cellulare e Genica, Rome, Italy
- King Faisal Specialist Hospital & Research Centre - Riyadh - Hematology, Al Mathar Ash Shamali, Saudi Arabia
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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