RecruitingPHASE1, PHASE2NCT06364774
ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia
Studying Beta-thalassemia
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Children's Hospital of Philadelphia
- Principal Investigator
- Janet Kwiatkowski, MD, MDChildren's Hospital of Philadelphia
- Intervention
- ALS20(biological)
- Enrollment
- 12 enrolled
- Eligibility
- 18-35 years · All sexes
- Timeline
- 2025 – 2027
Study locations (1)
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
Open NCT06364774 on ClinicalTrials.govOther trials for Beta-thalassemia
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