RecruitingPHASE1, PHASE2NCT05092685
Halting Ornithine Transcarbamylase Deficiency With Recombinant AAV in ChildrEn
Studying Ornithine transcarbamylase deficiency
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- University College, London
- Principal Investigator
- Federicco MingozziGenethon
- Intervention
- AAVLK03hOTC(genetic)
- Enrollment
- 12 enrolled
- Eligibility
- 16 years · All sexes
- Timeline
- 2023 – 2027
Study locations (1)
- Great Ormond Street Hospital, London, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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