Clinical trials for Ornithine transcarbamylase deficiency
8 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGNCT06805695Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)iECURE, Inc. · PI: George Diaz, M.D., Ph.D
- RECRUITINGPhase 2NCT06488313A Study to Evaluate the Pharmacodynamics and Safety of ARCT-810 in Participants With OTCDArcturus Therapeutics, Inc.
- RECRUITINGPHASE1, PHASE2NCT06255782An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC DeficiencyiECURE, Inc. · PI: George Diaz, M.D., Ph.D
- RECRUITINGPHASE1, PHASE2NCT05092685Halting Ornithine Transcarbamylase Deficiency With Recombinant AAV in ChildrEnUniversity College, London · PI: Federicco Mingozzi
- ACTIVE NOT RECRUITINGPhase 3NCT05345171Clinical Study of DTX301 AAV-Mediated Gene Transfer for Ornithine Transcarbamylase (OTC) DeficiencyUltragenyx Pharmaceutical Inc · PI: Medical Director
- RECRUITINGNCT04908319Hepatic Histopathology in Urea Cycle DisordersBaylor College of Medicine · PI: Lindsay Burrage, MD, PhD
- ACTIVE NOT RECRUITINGNCT04612764Liver Disease in Urea Cycle DisordersBaylor College of Medicine · PI: Lindsay Burrage, MD, PhD
- ACTIVE NOT RECRUITINGNCT03636438Long Term Follow Up to Evaluate DTX301 in Adults With Late-Onset OTC DeficiencyUltragenyx Pharmaceutical Inc · PI: Medical Director