RecruitingPHASE1, PHASE2NCT04774536
Transplantation of Clustered Regularly Interspaced Short Palindromic Repeats Modified Hematopoietic Progenitor Stem Cells (CRISPR_SCD001) in Patients with Severe Sickle Cell Disease
Studying Sickle cell disease
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Mark Walters, MD
- Principal Investigator
- Mark Walters, MD, MD, MPHUCSF Benioff Children's Hospital Oakland
- Intervention
- CRISPR_SCD001(drug)
- Enrollment
- 9 enrolled
- Eligibility
- 12-35 years · All sexes
- Timeline
- 2024 – 2029
Study locations (2)
- University of California, Los Angeles, Los Angeles, California, United States
- UCSF Benioff Children's Hospital, Oakland, California, United States
Collaborators
University of California, Los Angeles · University of California, Berkeley
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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