SuspendedPHASE1, PHASE2NCT04771416
Study of Safety, Tolerability and Efficacy of PBKR03 in Pediatric Subjects With Early Infantile Krabbe Disease
Studying Leukodystrophy
Last synced from ClinicalTrials.gov
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing dataKey facts
- Sponsor
- Gemma Biotherapeutics
- Principal Investigator
- May Orfali, MDGemma Biotherapeutics
- Intervention
- PBKR03(biological)
- Enrollment
- 24 enrolled
- Eligibility
- All sexes
- Timeline
- 2022 – 2030
Study locations (9)
- Ann & Robert Lurie, Chicago, Illinois, United States
- New York-Presbyterian, New York, New York, United States
- The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- University of Utah School of Medicine, Salt Lake City, Utah, United States
- Hospital De Clinicas De Porto Alegre, Porto Alegre, Brazil
- Montreal Children's Hospital, Montreal, Canada
- Shaare Zadek Medical Center, Jerusalem, Israel
- Amsterdam UMC, Amsterdam, Netherlands
- Manchester University, Manchester, United Kingdom
Primary source
Recruitment status, site addresses, contacts, and full eligibility criteria can change between syncs. Always verify with the trial team before planning travel or treatment.
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